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Tags: 2006, Backlog, Clinical Trials as Topic, Fadeel B, Hemophagocytic/drug therapy, Henter JI, Humans, Journal Article, Journal Of Internal Medicine, Lymphohistiocytosis, Orphan Drug Production/legislation & jurisprudence, Patient Advocacy, Rare Diseases/drug therapy, Severe Combined Immunodeficiency/drug therapy, Tyrosinemias/drug therapy, Wastfelt M
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